This program brings together the perspectives of renowned epileptologists, via survey and roundtable discussion, to assist practitioners in utilizing modern strategies for epilepsy assessment, integration of novel agents into routine practice, and therapeutic decision-making for difficult-to-treat epilepsies

This activity provides a case example of a patient with Duchenne Muscular Dystrophy (DMD), explains the genetic causes of DMD, and discusses the preliminary outcomes of 3 clinical trials using gene therapy to treat DMD.

Discuss the impact of poorly managed sickle cell disease on patient outcomes

In this clinical commentary, Kerry H. Hansen, RN, BS and Skye Peltier, MPH, PA-C review best practices to facilitate patient-centered hemophilia A prophylaxis management.

Formulate treatment plans to manage moderate-to-severe asthma in pediatric patients

Address challenging questions, make real-world decisions and assess expert guidance as you optimize diagnostic and therapeutic strategies for 3 families with a suspected rare disease, primary hyperoxaluria type 1 (PH1). 

Assess the severity of hemophilia A according to clinical presentation and results of factor assays