Duchenne Muscular Dystrophy: Recognizing Its Earliest Signs in Infancy and Care Transition into Adulthood
March 28, 2023
March 28, 2024
Jointly provided by Postgraduate Institute for Medicine and PlatformQ Health Education, LLC, working in collaboration with Parent Project Muscular Dystrophy (PPMD) and the National Organization for Rare Disorders (NORD).
This activity is supported by educational grants from PTC Therapeutics, Inc. and Sarepta Therapeutics, Inc..
- Physicians — maximum of 1.0 AMA PRA Category 1 Credit(s)™
All other healthcare professionals completing this course will be issued a statement of participation.
The intended audience for this activity are neurologists, neuromuscular specialists, pediatric neurologists, genetic counselors, and pediatricians.
Join a panel of expert clinicians to identify the subtle and very early signs of DMD that may be detected before functional symptoms are noticed and that can help earlier diagnoses and appropriate interventions. Panelists will review the importance of matching mutations to therapeutic decisions, discuss emerging concepts around functional and non-functional outcomes of treatment success, and share strategies to optimize care related to mood, bone health, and transitions from pediatric to adult care.
Upon completion of this activity, participants should be better able to:
- Summarize the early signs of muscle injury that often precede development of visible symptoms in DMD
- Define how genetic testing can influence treatment decisions
- Explain how early treatment with DMTs can alter the natural history of DMD
- Examine functional and non-functional outcomes and how they influence the definition of treatment success
- Identify components of multidisciplinary care for patients with DMD, including optimizing mood, bone health, and plans to transition from pediatric to adult care
John Brandsema, MD
Neuromuscular Section Head
Children’s Hospital of Philadelphia
Emma Ciafaloni, MD
Professor of Neurology and Pediatrics
University of Rochester
Joint Accreditation Statement
In support of improving patient care, this activity has been planned and implemented by the Postgraduate Institute for Medicine and PlatformQ Health Education, LLC. Postgraduate Institute for Medicine is jointly accredited by the Accreditation Council for Continuing Medical Education (ACCME), the Accreditation Council for Pharmacy Education (ACPE), and the American Nurses Credentialing Center (ANCC), to provide continuing education for the healthcare team.
Physician Credit Designation
The Postgraduate Institute for Medicine designates this enduring material for a maximum of 1.0 AMA PRA Category 1 Credit™. Physicians should claim only the credit commensurate with the extent of their participation in the activity.
Disclosures of Conflicts of Interest
Postgraduate Institute for Medicine (PIM) requires instructors, planners, managers and other individuals who are in a position to control the content of this activity to disclose any real or apparent conflict of interest (COI) they may have as related to the content of this activity. All identified COI are thoroughly vetted and resolved according to PIM policy. PIM is committed to providing its learners with high quality CME activities and related materials that promote improvements or quality in healthcare and not a specific proprietary business interest of a commercial interest.
The faculty reported the following financial relationships or relationships to products or devices they or their spouse/life partner have with commercial interests related to the content of this CME activity:
- John Brandsema, MD
- Grant/Research Support: Alexion, Astellas, AveXis/Novartis, Biogen, CSL Behring, Fibrogen, Genentech, Pfizer, PTC Therapeutics, Sarepta
- Consultant/Advisory Board: AveXis/Novartis, Biogen, Genentech, Janssen, Pfizer, PTC Therapeutics, Sarepta
- Emma Ciafaloni, MD
- Grant/Research Support: Sarepta
- Consultant/Advisory Board: Alexion, Sarepta
The planners and managers reported the following financial relationships or relationships to products or devices they or their spouse/life partner have with commercial interests related to the content of this CME activity:
Carole Drexel, Medical Director, PlatformQ Health Education, LLC, has nothing to disclose.
Vandana Gupta, Medical Director, PlatformQ Health Education, LLC, has nothing to disclose.
The PIM planners and managers have nothing to disclose.
The following PlatformQ Health Education, LLC planner, Jaimee Harris-Gold, hereby states that she or her spouse/life partner do not have any financial relationships or relationships to products or devices with any commercial interest related to the content of this activity of any amount during the past 12 months.
Method of Participation
There are no fees to participate in this activity. To participate in the activity, go to www.NeuroSeriesLive.com. To receive credit, participants must (1) read the target audience, learning objectives, and disclosure statements, (2) complete the educational activity online, and (3) complete the post-test and activity evaluation. To receive AMA PRA Category 1 Credit™, participants must receive a minimum score of 70% on the post-test.
Course Viewing Requirements
Internet Explorer 8.0+ for Windows 2003, Vista, XP, Windows 7, Windows 8.1 and above
Google Chrome 28.0+ for Windows, Mac OS, or Linux
Mozilla Firefox 23.0+ for Windows, Mac OS, or Linux
Safari 6.0+ for Mac OSX 10.7 and above
Supported Phones & Tablets:
Android 4.0.3 and above
iPhone/iPad with iOS 6.1 or above
Disclosure of Unapproved/Off Label Use (if applicable)
This educational activity may contain discussion of published and/or investigational uses of agents that are not indicated by the FDA. The planners of this activity do not recommend the use of any agent outside of the labeled indications.
The opinions expressed in the educational activity are those of the faculty and do not necessarily represent the views of the planners. Please refer to the official prescribing information for each product for discussion of approved indications, contraindications, and warnings.
Participants have an implied responsibility to use the newly acquired information to enhance patient outcomes and their own professional development. The information presented in this activity is not meant to serve as a guideline for patient management. Any procedures, medications, or other courses of diagnosis or treatment discussed or suggested in this activity should not be used by clinicians without evaluation of their patient’s conditions and possible contraindications and/or dangers in use, review of any applicable manufacturer’s product information, and comparison with recommendations of other authorities.
Please contact the Postgraduate Institute for Medicine at [email protected].
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